Thank you for attending this year’s Achondroplasia Research Conference presented by The Chandler Project!
This year, attendees heard from world-renowned skeletal dysplasia experts who are leaders in research and surgical advancements for those living with achondroplasia and other forms of dwarfism/skeletal dysplasia. This annual event is the only one of its kind in North America that brings together affected individuals living with a form of skeletal dysplasia, parents, caregivers, physicians, and researchers to engage with one another and learn about what's happening now and what's to come for future generations. Please visit this page and/or thechandlerproject.org frequently for updates on future events and conferences.
Access to the recorded sessions* (almost 7 hours of content!) is now available. For those who attended the conference this year, the recorded sessions can be found under the recordings tab. If you did not attend the conference or did not register prior to June 18, you can register here to access the recordings. Please note, there is a fee.
*BioMarin's session, Starting VOXZOGO® (vosoritide) for Injection: One Family’s Story, was not recorded. For information pertaining to VOXZOGO®, please visit VOXZOGO.com to discover how it works, sign up for events and more.
Day 1 Sessions
Diagnostic and Therapeutic Approach in the Growth Hormone Era
Dr. Andrew Dauber, Chief of Endocrinology
Children's National Hospital
First in Class Transformative Therapies for Patients with Rare Bone Disorders
Samantha Parker, Chief Patient Access Officer
InnoSkel
New Precision Therapies for FGFR3-Related Skeletal Dysplasia
Professor Ravi Savarirayan MB, BS (Adel.); MD (Melb.); FRACP; ARCPA (Hon.), Group Leader of Skeletal Therapies
Murdoch Children's Research Institute
Day 2 Morning Sessions
CLARITY: Achondroplasia Natural History Study
Dr. Jeffrey Campbell, Pediatric Neurosurgery
Nemours Children's Hospital
The Spine in Achondroplasia: Why Treat? Why Fuse?
Dr. David Feldman, Associate Director
Paley Orthopedic & Spine Institute at St. Mary's Medical Center
Orthopedic Care for Achondroplasia
Dr. Philip McClure, Assistant Director
International Center for Limb Lengthening, Rubin Institute for Advanced Orthopedics at Sinai Hospital
Limb Lengthening for Achondroplasia
Dr. Shawn Standard, Head of Pediatric Orthopedics
International Center for Limb Lengthening, Rubin Institute for Advanced Orthopedics at Sinai Hospital
Day 2 Afternoon Sessions
Development of Recifercept: Potential for Use in Achondroplasia
Alison Slade, GCL & Clinician
Rare Disease Research Unit, Pfizer
Targeting FGFR in Achondroplasia and Other FGFR-Driven Skeletal Dysplasia
Carl Dambkowski, MD
Chief Medical Officer, QED Therapeutics
Ascendis Pharma's Commitment to Achondroplasia
Adebola Giwa, MD
Associate Medical Director of Clinical Development, Ascendis Pharma
Panel Q&A
Facilitated by Dr. Cathleen Raggio, Co-Director
The Katrhyn O. and Alan C. Greenberg Center for Skeletal Dysplasias, Hospital for Special Surgery
